Massachusetts is home to a thriving pharmaceutical industry, with leading companies pushing the boundaries of drug discovery and biopharmaceutical advancements. From cannabinoid-based therapies by Targeted Pharmaceuticals in Worcester to oncology-focused innovations by TESARO in Waltham, these firms are at the forefront of cutting-edge research in personalized medicine and biotech. Investment opportunities abound in sectors such as oncology, neurology, and antimicrobial resistance, driven by Massachusetts' robust ecosystem of publicly traded companies and dynamic startups.
Targeted Pharmaceuticals specializes in cannabinoid-based drug discovery and personalized medicine within the pharmaceutical manufacturing industry, focusing on innovative approaches to developing tailored therapeutic solutions.
Engaged in biotechnology research, Synspira Therapeutics focuses on innovative therapeutic solutions, emphasizing advancements in treatment methodologies.
Aurora Biopharma, Inc. specializes in research services within the biopharmaceutical industry, focusing on innovative approaches to drug development and therapeutic solutions.
Dyax specializes in biotechnology research, focusing on innovative approaches to develop therapies for rare diseases. Its expertise in this niche area enhances its contributions to the biotechnology industry.
Mispro specializes in providing AAALAC-accredited contract vivarium services for preclinical rodent studies, catering to biopharmaceutical research organizations with comprehensive animal care and compliance solutions. Its innovative approach includes offering dedicated vivarium space and specialized services that enhance the efficiency of biomedical and pharmaceutical research.
Ra Pharmaceuticals specializes in pharmaceutical manufacturing, focusing on innovative therapies for rare diseases. Its unique approach includes the development of peptide-based treatments, enhancing the effectiveness and precision of drug delivery.
Trevie Research specializes in oncology-focused clinical development and trial management, offering expert advisory services in biopharma drug development and commercialization. The firm leverages extensive experience and strong relationships with key opinion leaders to support Phase I/II drug development programs for biotech, pharmaceutical, and non-profit organizations.
Prilenia is a clinical-stage biotechnology firm dedicated to developing innovative treatments for neurodegenerative and neurodevelopmental disorders, with a focus on its lead asset, Pridopidine, a first-in-class oral drug candidate. The firm is actively conducting advanced clinical trials for Huntington’s disease and ALS, leveraging an established safety profile to address significant unmet medical needs.
Oxeia Biopharmaceuticals is focused on developing innovative therapeutics for mild traumatic brain injury (concussion) and related neuro-metabolic dysfunction, with a clinical-stage drug, OXE103, currently undergoing Phase 2 trials. Their unique approach addresses a significant gap in treatment options for concussion patients, emphasizing the need for more than just rest.
Bach Pharma operates in the biotechnology industry, focusing on innovative solutions for pharmaceutical development and production. Their unique approach emphasizes advanced biotechnological methods to enhance drug efficacy and safety.
NeuForm Pharmaceuticals specializes in innovative drug discovery within the biopharmaceutical sector, developing proprietary and patent-protected candidates targeting oncology, neurology, immunology, and metabolic diseases. The organization emphasizes collaboration with top academic and clinical experts to deliver best-in-class medicines to patients.
NeuroSense Therapeutics is a clinical-stage biotechnology firm dedicated to advancing innovative treatments for ALS and other neurodegenerative diseases, employing a rigorous approach through its Phase 2b clinical study. Its focus on developing groundbreaking therapies positions it at the forefront of the biopharmaceutical industry.
Focused on the discovery and development of treatments for neurodegenerative diseases, this pharmaceutical manufacturer specializes in addressing conditions such as ALS, employing a collaborative approach to enhance the lives of those affected.
Specializing in biotechnology research, this organization offers innovative, customized solutions for clinical research, focusing on strategic planning and regulatory compliance to enhance the efficiency of drug development programs. With over 20 years of experience, it emphasizes simplified clinical trial designs and evidence-based strategies to maximize success and reduce risks for biotech and pharmaceutical clients.
NeuroCores, Inc. is a preclinical-stage biopharmaceutical firm specializing in the development of treatments for rare pediatric neurological and neurodegenerative disorders. Its innovative approach includes the use of plasmalogen derivatives, which exhibit strong anti-neuroinflammatory and neurogenesis effects, positioning the firm as a leader in addressing critical unmet medical needs in this niche market.
DecImmune Therapeutics, Inc. operates in the biotechnology industry, focusing on innovative therapeutic solutions. Their unique approach emphasizes the development of advanced treatments for immune-related diseases.
Clinical Trials 365 provides daily news and updates on pharmaceutical and biopharmaceutical clinical trials, focusing on delivering timely and relevant information in the rapidly evolving healthcare sector. Its innovative approach keeps stakeholders informed about the latest developments in clinical research.
Akashi Therapeutics is a clinical stage biotechnology firm focused on developing innovative therapies for Duchenne muscular dystrophy and other rare diseases, with a strong emphasis on muscle regeneration and anti-inflammatory properties through its lead asset HT-100 and the muscle-building SARM DT-200. The organization is distinguished by its foundation through collaboration between patient advocacy groups and seasoned biotechnology professionals.
Eloxx Pharmaceuticals is a clinical-stage biopharmaceutical firm specializing in the development of innovative RNA-modulating drug candidates aimed at treating rare and ultra-rare diseases caused by premature stop codons. Their lead product, ELX-02, is designed to enhance protein synthesis by enabling ribosomes to bypass these genetic mutations, addressing significant challenges in conditions like cystic fibrosis and cystinosis.
Arsanis specializes in biotechnology research, focusing on innovative solutions in the pharmaceutical sector. The firm is positioned for growth following its merger with X4 Pharmaceuticals, enhancing its capabilities in developing advanced therapeutic options.
Oncoheroes Biosciences is dedicated to advancing innovative therapies for childhood cancer through the identification and development of promising drug projects. Its specialized focus on drug and clinical development positions it uniquely in the life sciences sector.
A clinical-stage biopharmaceutical entity specializing in the development of innovative therapies for oncology, dermatology, and antimicrobial applications, with a focus on small molecule treatments. Key drug candidates include Kevetrin for cancer, Prurisol for psoriasis, and Brilacidin, a defensin-mimetic aimed at treating skin infections and complications from cancer therapies.
Javelin Biotech specializes in biotechnology research, developing predictive drug discovery platforms that integrate human and computational biology to enhance preclinical drug discovery and increase drug approval rates.
A national medical specialty society dedicated to promoting best practices in pharmacovigilance, focusing on the detection and prevention of drug-related adverse effects. It offers training programs and co-sponsors conferences, catering to physicians and clinicians in the pharmaceutical and biotech industries.
Atea Pharmaceuticals is a clinical-stage biopharmaceutical firm focused on discovering and developing innovative antiviral therapies for COVID-19 and severe viral diseases, addressing critical unmet medical needs in the biotechnology research industry.
Cerevance specializes in biotechnology research, focusing on innovative approaches to drug discovery and development. Their unique methodologies aim to advance treatments for neurological disorders, setting them apart in the biotech industry.
A leading nonprofit in biotechnology research, this organization is dedicated exclusively to discovering and developing treatments for amyotrophic lateral sclerosis (ALS). It is recognized for its innovative approach to drug discovery, leveraging expertise from both industry professionals and individuals affected by ALS to advance preclinical and translational research.
A clinical-stage biopharmaceutical firm specializing in the research and development of innovative therapeutics for rare hematologic diseases and cancers, leveraging deep biological insights and chemistry expertise to create drug candidates with unique mechanisms of action to address high unmet medical needs.
Wild Biotech is a biotechnology research firm specializing in drug discovery, leveraging innovative approaches to develop resilient therapeutic solutions.
Pharmagellan provides expert consulting services in R&D strategy for the biotech, pharmaceutical, and medical device sectors, offering industry-leading insights on biotech finance and clinical trial analysis. Their focus on senior advisory roles positions them as trusted partners for firms and investors navigating complex research and development landscapes.
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